The translational gap for gene therapies in low- and middle-income countries

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dc.contributor.authorDoxzen K.W.
dc.contributor.authorAdair J.E.
dc.contributor.authorBazzo Y.M.F.
dc.contributor.authorBukini D.
dc.contributor.authorCornetta K.
dc.contributor.authorDalal V.
dc.contributor.authorGuerino-Cunha R.L.
dc.contributor.authorHongeng S.
dc.contributor.authorJotwani G.
dc.contributor.authorKityo-Mutuluuza C.
dc.contributor.authorLakshmanan K.
dc.contributor.authorMahlangu J.
dc.contributor.authorMakani J.
dc.contributor.authorMathews V.
dc.contributor.authorOzelo M.C.
dc.contributor.authorRangarajan S.
dc.contributor.authorScholefield J.
dc.contributor.authorJúnior J.B.S.
dc.contributor.authorMcCune J.M.
dc.contributor.correspondenceDoxzen K.W.
dc.contributor.otherMahidol University
dc.date.accessioned2024-05-20T18:15:24Z
dc.date.available2024-05-20T18:15:24Z
dc.date.issued2024-05-08
dc.description.abstractGene therapies are designed to address the root cause of disease. As scientific understanding of disease prevention, diagnosis, and treatment improves in tandem with technological innovation, gene therapies have the potential to become safe and effective treatment options for a wide range of genetic and nongenetic diseases. However, as the medical scope of gene therapies expands, consideration must be given to those who will benefit and what proactive steps must be taken to widen development and access potential, particularly in regions carrying a high disease burden.
dc.identifier.citationScience translational medicine Vol.16 No.746 (2024) , eadn1902
dc.identifier.doi10.1126/scitranslmed.adn1902
dc.identifier.eissn19466242
dc.identifier.pmid38718130
dc.identifier.scopus2-s2.0-85192633925
dc.identifier.urihttps://repository.li.mahidol.ac.th/handle/20.500.14594/98372
dc.rights.holderSCOPUS
dc.subjectMedicine
dc.titleThe translational gap for gene therapies in low- and middle-income countries
dc.typeReview
mu.datasource.scopushttps://www.scopus.com/inward/record.uri?partnerID=HzOxMe3b&scp=85192633925&origin=inward
oaire.citation.issue746
oaire.citation.titleScience translational medicine
oaire.citation.volume16
oairecerif.author.affiliationFred Hutchinson Cancer Center
oairecerif.author.affiliationAgência Nacional de Vigilância Sanitária, Brazil
oairecerif.author.affiliationMuhimbili University of Health and Allied Sciences
oairecerif.author.affiliationUniversity of the Witwatersrand Faculty of Health Sciences
oairecerif.author.affiliationJoint Clinical Research Center Uganda
oairecerif.author.affiliationMinistry of Health and Family Welfare
oairecerif.author.affiliationUniversidade Estadual de Campinas
oairecerif.author.affiliationIndian Council of Medical Research
oairecerif.author.affiliationUniversity of Southampton, Faculty of Medicine
oairecerif.author.affiliationUniversidade de Brasília
oairecerif.author.affiliationBill & Melinda Gates Foundation
oairecerif.author.affiliationIndiana University School of Medicine
oairecerif.author.affiliationYale School of Medicine
oairecerif.author.affiliationFaculty of Medicine Ramathibodi Hospital, Mahidol University
oairecerif.author.affiliationUniversity of Washington
oairecerif.author.affiliationImperial College London
oairecerif.author.affiliationThe Council for Scientific and Industrial Research
oairecerif.author.affiliationFaculty of Health Sciences
oairecerif.author.affiliationChristian Medical College, Vellore
oairecerif.author.affiliationHaematology & Rare Disorders (ACOHRD)
oairecerif.author.affiliationRJ
oairecerif.author.affiliationCentro Paulista de Oncologia
oairecerif.author.affiliationStrategic Analysis, Inc.

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