Identifying thresholds for meaningful improvements in NTDT-PRO scores to support conclusions about treatment benefit in clinical studies of patients with non-transfusion-dependent beta-thalassaemia: analysis of pooled data from a phase 2, double-blind, placebo-controlled, randomised trial

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Taher A.T., Musallam K.M., Viprakasit V., Kattamis A., Lord-Bessen J., Yucel A., Guo S., Pelligra C.G., Shields A.L., Shetty J.K., Glassberg M.B., Bueno L.M., Cappellini M.D. Identifying thresholds for meaningful improvements in NTDT-PRO scores to support conclusions about treatment benefit in clinical studies of patients with non-transfusion-dependent beta-thalassaemia: analysis of pooled data from a phase 2, double-blind, placebo-controlled, randomised trial. BMJ open Vol.14 No.11 (2024) , e085234. doi:10.1136/bmjopen-2024-085234 Retrieved from: https://repository.li.mahidol.ac.th/handle/123456789/102202

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